Tag: NFIB

Lebers congenital amaurosis (LCA) is a group of severe inherited retinal degenerations that are symptomatic in infancy and lead to total blindness in adulthood. complementary DNA (cDNA) into one attention of LCA individuals with mutations in (referred to as LCA-RPE65 subjects) using recombinant adeno-associated disease serotype 2 (rAAV2) vectors ( 0.0001, 2 evaluation). At baseline,…